Welcome to Novartis Gene Therapies Medical Information

Novartis Gene Therapies Medical Information is committed to providing the most up‑to‑date, accurate, and balanced scientific information regarding Novartis Gene Therapies products.

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Managed Access Program
Patients with serious or life-threatening diseases or conditions sometimes seek medical products that are not yet approved or available in their country. Novartis Gene Therapies’ “Managed Access” addresses this need by making certain unlicensed or unapproved treatments available to eligible patients. Click here to learn more.

Visitors Outside Asia-Pacific
This website is intended for residents of the Asia-Pacific region. If you are outside of this region, please visit our Global page. Inquiries from Japan are being handled by our Novartis partners. If you are a resident of Japan, click here to access the Novartis Japan site or click here to submit an inquiry.

About Novartis Gene Therapies
Novartis Gene Therapies is a Novartis company dedicated to developing and commercializing gene therapies for patients and families devastated by rare and life-threatening neurological genetic diseases. Click here for more information.