Patient Resources

The OneGene Program is a team of highly trained and dedicated people who help ensure that every family has the support they need during their treatment journey and beyond.  For questions about cost, ordering, reimbursement, and patient support resources, please click here or call +1-855-441-4363 (1-855-441-GENE) for information.

Managed Access Program

The Novartis Gene Therapies “Managed Access Program” terminology covers all locally defined pre-approval access mechanisms and programs such as “Compassionate Use”, “Expanded Access”, “Named Patient Supply”, “Special Access Schemes/Programs”, “Autorisations temporaires d’utilisation (ATU)” and others. Click here for more information about our Managed Access Program.