Novartis Gene Therapies has a wide array of resources for caregivers, patients, and advocacy groups. To learn more, please click on the section of interest below or scroll down to browse.

Novartis Resources

Click here for information on Novartis Gene Therapies and our commitment to SMA and gene therapy products and pipeline. To learn more about Novartis clinical trials and other resources, please click below:

Clinical Trial Resources is a database of privately and publicly funded clinical studies conducted around the world.

Safety Resources

The following external resources offer general information on safety. Please note that clicking on the following websites will take you outside of Novartis Gene Therapies Medical Information site.

Patient Organizations

The following organizations offer resources and information for patients and loved ones impacted by rare disorders.

For additional patient community resources for rare disorders, please click here.