Scientific Congresses

World Muscle Society Congress 2024

October 8-12, 2024

Poster presentations:

Darras BT, Farrar MA, Mercuri E, et al. Intravenous and intrathecal onasemnogene abeparvovec gene therapy in symptomatic and presymptomatic spinal muscular atrophy: long-term follow-up study. Poster presented at the 29th Annual Congress of the World Muscle Society, October 8-12, 2024; Prague, Czechia.

Reyna S, Toro W, Patel A, Saleh S, Dabbous O. Health care resource use for patients with spinal muscular atrophy types 2 or 3 in the United Kingdom. Poster presented at the 29th Annual Congress of the World Muscle Society, October 8-12, 2024; Prague, Czechia.

Reyna SP, Dabbous O, Wallach S, et al. Meta-analysis of clinical impact of onasemnogene abeparvovec treatment of spinal muscular atrophy patients. Poster presented at the 29th Annual Congress of the World Muscle Society, October 8-12, 2024; Prague, Czechia.

Servais L, Alecu I, Lopwz-Leon S, et al. Long-term safety of onasemnogene abeparvovec for patients with spinal muscular atrophy: real-world findings from the RESTORE registry. Poster presented at the 29th Annual Congress of the World Muscle Society, October 8-12, 2024; Prague, Czechia.

Servais L, Shieh PB, Goedeker NL, et al. Real-world outcomes following onasemnogene abeparvovec in patients with SMA and invasive ventilatory support: findings from the RESTORE registry. Poster presented at the 29th Annual Congress of the World Muscle Society, October 8-12, 2024; Prague, Czechia.

Servais L, Mathews K, Bernes S, et al. Real-world outcomes following onasemnogene abeparvovec in patients with SMA and one SMN2 gene copy: findings from the RESTORE registry. Poster presented at the 29th Annual Congress of the World Muscle Society, October 8-12, 2024; Prague, Czechia.

Zanoteli E, Muntadas J, Gurgel-Gianetti J, et al. Safety and tolerability of onasemnogene abeparvovec for patients with spinal muscular atrophy weighing ≤24 months old: phase 4 OFELIA study. Poster presented at the 29th Annual Congress of the World Muscle Society, October 8-12, 2024; Prague, Czechia.